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Amyloid Neuropathies, Familial - 22 Studies Found
Estado | Estudiar |
Enrolling by invitation |
Nombre del estudio: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Patients Who Have Already Been Treated With ALN-TTR02 (Patisiran) Condición: Amyloidosis Fecha: 2015-07-16 Intervenciones: Drug: Patisiran (ALN-TTR02) administered by intravenous (IV) infusion |
Completed |
Nombre del estudio: Burden of Disease Study In Patients With Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) orTransthyretin Cardiomyopathy (TTR-CM) And Caregivers Condición:
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